Gene Therapy in Drug Development: Advancements, Challenges, and Future Perspectives

Abstract

Gene therapy has emerged as a promising approach to developing novel therapeutics, offering the potential for treating a wide range of genetic disorders, cancers, and other diseases. This review provides an overview of the advancements in gene therapy, including the key technologies, delivery systems, regulatory frameworks, and challenges that influence its integration in drug development. The current state of gene therapy-based products in clinical trials and their impact on pharmaceutical development are also discussed, emphasizing future directions.